Quest Winter 2014

January 1, 2014 - March 31, 2014

Cover Story

A strong support system makes it possible for one gifted student with Duchenne muscular dystrophy to pursue his dreams

Raymond Walter isn’t your typical teenager. Having graduated from high school at age 14 and from college at 18, he’s already knee-deep in his doctoral studies in mathematics and physics as a Distinguished Doctoral Fellow and a National Science Foundation Graduate Research Fellow at the University of Arkansas at age 19. 

Features

Hansell Stedman, a surgeon who had two brothers with Duchenne muscular dystrophy, aims to translate lessons from crush injuries into improvements in gene therapy
Charles Gersbach is using “nuclease-based genome correction” to turn flawed dystrophin genes into functional ones
Researcher Carmen Bertoni is using DNA-like material to fix flawed genes
A look at how today's gene therapy research for DMD is overcoming obstacles
The Abilities Expo, held in seven U.S. cities annually, offers a peek at new assistive technology and trends as well as product test-drives
Taking more than care
Jeffrey Chamberlain believes that providing new dystrophin genes is the best way to treat Duchenne muscular dystrophy, although combining gene transfer with other strategies interests him.
MDA re-launches its flagship publication, with a fresh look and the same high-quality content for people living with muscle disease
Dongsheng Duan is tweaking dystrophin genes to improve their therapeutic efficacy, designing better viral vectors in which to package the genes, and aims to treat the heart with gene transfer

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Quest Extra

The author’s weight loss surgery led her to start an exercise program that provided her with more muscle tone — and a lot of fun