How the FDA tries to balance urgent needs against real risks when evaluating new drugs
posted on April 1, 2013 - 9:25am
The approval of new drugs in the United States is a complex process that seeks to balance the need to protect the health and safety of the population with the need to provide treatment as soon as possible for serious or life-threatening disorders.
MDA advocacy in Washington
posted on April 1, 2013 - 9:23am
I have had the great privilege of witnessing some of the most transformative legislative moments in our MDA community’s history. While we have many heroes and legends among us, there are also many heroes whose names most will never know — people who, through their outreach to their elected officials, brought great champions to the cause of neuromuscular disease research and services.
What’s ready now and what’s in your future
posted on April 1, 2013 - 9:21am
Entering into the world of disability should come with a giant neon sign that reads “Warning: Technology Ahead.” It’s inescapable. Not only is it all around us but for many of us, technology keeps us alive well beyond what the naysayers predict.
Different neuromuscular diseases progress at different rates, but eventually we all start losing mobility, strength and/or dexterity. Some of us will...
On being treated as a person first during hospitalizations
posted on April 1, 2013 - 9:19am
MJ Purk
Individuals with neuromuscular disorders oftentimes spend a great deal of time in the hospital and even more time interacting with those who work in the medical profession. In their interactions with medical personnel, some individuals are lucky enough to experience more than the expected amount of caring.
The right cushion makes all the difference in wheelchair comfort
posted on April 1, 2013 - 9:17am
Anyone using a wheelchair, even for a few hours a day, needs to sit on a cushion. The most obvious reason for using a wheelchair cushion is simply to offer general comfort by reducing friction and vibration. A good cushion also can wick away moisture and keep you cool.
posted on April 1, 2013 - 9:15am
Note: Click on photos to enlarge.
Moving Toward 'Next-Generation' Gene Therapy - 05/23/13
FA: RG2833 is Well-Tolerated and Increases Frataxin Gene Activity - 05/17/13
Newborn Screening Recommended for Pompe Disease - 05/17/13
DMD, BMD: Phase 3 Trial Opens for Stop Codon Read-Through Drug - 05/08/13
SMA: Trial Tests Antisense Therapy in Infants - 05/07/13
MTM Phone-Based 'Event' Study Now Open - 05/03/13
