Weekly injections of the exon-skipping drug drisapersen in boys with Duchenne muscular dystrophy resulted in a significant difference in walking distance compared to a placebo

posted on April 11, 2013 - 11:59am

Investigators are testing compounds designed to cause exon skipping in Duchenne MD and drugs that may increase blood flow in Duchenne and Becker MD

posted on June 21, 2011 - 9:08am
U.S. trial of eteplirsen for Duchenne MD delayed