trial results

Drisapersen-treated trial participants with Duchenne MD had higher levels of dystrophin protein in their muscle samples at 25 weeks than did placebo-treated participants

posted on August 21, 2013 - 12:17pm
Multinational pharmaceutical company GlaxoSmithKline (GSK) has released encouraging results about dystrophin protein production in a phase 2, non-U.S. trial of its exon-skipping compound drisapersen in boys with Duchenne muscular dystrophy (DMD).
posted on October 1, 2001 - 12:30pm
As progress toward treatment grows, keeping track of clinical trials in neuromuscular diseases has become more important — and more daunting — than ever. These days, it's fairly easy to find scientific reports about clinical trials, but wading through the technical jargon in those reports can be difficult. If you're considering enrolling in a clinical trial, you'll probably want to understand the...