A strategy to repair DNA in cells taken from boys with Duchenne muscular dystrophy has resulted in production of dystrophin protein molecules

posted on June 11, 2013 - 2:05pm
Permanent repair of a faulty gene has long been a goal of researchers working to develop gene-based therapies. But many current gene modification strategies that have entered clinical trials have been based on temporary forms of gene correction — treatments that will need to be given frequently throughout a person's life.

New content is being added every day. Please check back again.