replacement therapy

Four children not making any acid maltase enzyme tolerated enzyme replacement therapy when also treated with immunosuppressants

posted on January 16, 2012 - 6:00am
Editor's note 2/2/12: This story was updated to reflect the award of a  new MDA grant to Eric Sjoberg at Amicus Therapeutics. Drugs that suppress the immune system can successfully prevent or reverse rejection of enzyme replacement therapy in Pompe disease (acid maltase deficiency), a new study has shown.

New content is being added every day. Please check back again.