presymptomatic SMA

MDA-supported scientists found raising SMN protein levels conferred significant benefits on young SMA mice, even after symptom onset

posted on August 4, 2011 - 9:40am
The "window of opportunity" for treating infants at risk of developing spinal muscular atrophy (SMA) may not be as narrow as some experts have feared, new experiments in mice suggest.
posted on May 1, 2008 - 10:21am
QUEST Vol. 15, No. 3
This article includes items about: Duchenne muscular dystrophy, limb-girdle muscular dystrophy, Becker muscular dystrophy, myotonic muscular dystrophy, fascioscapulohumeral muscular dystrophy, Charcot-Marie-Tooth disease, spinal muscular atrophy, Friedreich's ataxia, myasthenia gravis and centronuclear myopathy