Featured in this issue: Disappointing results from ataluren trial leads to further analysis * First U.S. site for idebenone in DMD trial opens * Utrophin-boosting drug begins safety tests * Participants sought for trials in DMD, CMD, myotonic distrophy and periodic paralysis
Study of PGD seeks couples who said 'no'
New muscle-generating stem cells isolated from human tissue
Researchers at several U.S. and Italian institutions say they’ve isolated from human skeletal muscle a new type of stem cell that they believe could be “ideal” for the treatment of muscular dystrophy.
MDA-supported Giulio Cossu at the San Raffaele Scientific Institute in Milan, Italy, and Paolo Bianco of the San Raffaele Biomedical...