gene delivery

An update on stem cell research related to neuromuscular disease as of July 2009

posted on July 1, 2009 - 5:17pm
Stem cells — immature cells with the potential to develop into different tissue types — have been heralded as a major advance for developing treatments for a variety of diseases. That’s true for diseases of the nerves and muscles, where such cells could potentially be transplanted into the body and either support or replace a patient’s ailing cells.
posted on January 1, 2009 - 3:48pm
QUEST Vol. 16, No. 1
Story includes research items about: centronuclear myopathy; Duchenne, limb-girdle, and Emery-Dreifuss muscular dystrophies; and spinal muscular atrophy.
posted on January 1, 2007 - 11:54am
QUEST Vol. 14, No. 1
Gene therapy — inserting new genes into cells to treat disease — first became a reality in the early 1990s. Now past its earliest years and into its adolescence, the science has progressed along two major pathways. The first seeks to define the best way of delivering genes inside the shell of a defanged virus, with the precise type of viral shell dependent on the target tissue. Viral delivery...
posted on March 1, 2005 - 10:55am
In this article: research news about prednisone in Duchenne MD; tests for Duchenne and Becker MDs; and the latest progress in research for spinal muscular atrophy