DMD natural history

Prosensa and GlaxoSmithKline aim to enroll 250 participants in a study to determine the usual progression of Duchenne muscular dystrophy and aid clinical trials

posted on November 14, 2013 - 11:01am
Update (June 25, 2014): Prosensa announced in a June 25, 2014, press release that it has completed enrollment for this natural history study. The study is no longer open to new participants. The study is expected to be completed in November 2017, but an interim analysis is expected later in 2014. Update (Jan. 27, 2014): Prosensa is now the sole sponsor of this study. original story:

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