animal testing

What can laboratory studies tell us about human disease?

posted on July 1, 2005 - 2:39pm
QUEST Vol. 12, No. 4
This spring, the Duchenne muscular dystrophy community rejoiced when PTC Therapeutics of South Plainfield, N.J., announced that an experimental drug aimed at the disease had passed safety tests in human volunteers and would now be tested in boys with DMD. This drug, like many others, was successfully tested in mice lacking dystrophin, the protein that’s also missing in the human form of the...