MDA and AFM co-sponsored a symposium on neuromuscular gene therapy at the 2012 meeting of the American Society for Gene & Cell Therapy
posted on May 22, 2012 - 2:25pm
Overcoming barriers to gene therapy — the delivery of therapeutic genes — to treat neuromuscular diseases was the topic of a symposium jointly sponsored by MDA and the Association Française Contre les Myopathies (French Association Against Myopathies, or AFM) at the 15th annual meeting of the American Society of Gene & Cell Therapy (ASGCT).
Wake Forest researcher receives $369,365 for preclinical testing of gene transfer therapy for myotubular myopathy
posted on May 26, 2011 - 2:16pm
MDA’s translational research program has announced it is funding research into a potential treatment for the inherited muscle disorder X-linked myotubular myopathy (MTM).
The grant of $369,365 grant to Wake Forest University professor Martin Childers will fund a three-year study of myotubularin gene transfer in mice and dogs that have an MTM-like disease.
This article includes items about research in: Duchenne MD, limb-girdle MD, inclusion-body myositis, polymyositis, dermatomyositis, FSH dystrophy, myotonic muscular dystrophy and researcher George Karpati.