RNAi

Innovative research aims to deepen understanding of the molecular cause of FSHD, with the goal of developing therapies

posted on April 5, 2010 - 5:23pm
MDA has awarded two grants for research aimed at determining the precise molecular causes of facioscapulohumeral dystrophy (FSHD), and developing therapies for the disease. MDA and Friends of FSH Research (FFSHR) based in Kirkland, Wash., will jointly fund a two-year, $200,000 grant to Joel Chamberlain, an assistant professor of medical genetics at the University of Washington in Seattle.

Can toxic genes be blocked to treat disease?

posted on January 1, 2007 - 3:02pm
QUEST Vol. 14, No. 1
Since the 1990s, gene therapy - the insertion of functional genes to compensate for nonfunctional ones - has been the goal of researchers working in several muscular dystrophies, spinal muscular atrophy, Friedreich's ataxia, metabolic muscle diseases and myotubular myopathy.