RNA interference

An ALS compound that's ready for biotech development is described in this Oct. 5, 2009, Webcast

posted on October 18, 2009 - 9:00pm
A Webcast is now available of the fourth annual research symposium held as part of the ALS TDI Leadership Summit 2009 on Oct. 5. The symposium was conducted at the MDA-supported ALS Therapy Development Institute in Cambridge, Mass.

Can toxic genes be blocked to treat disease?

posted on January 1, 2007 - 3:02pm
QUEST Vol. 14, No. 1
Since the 1990s, gene therapy - the insertion of functional genes to compensate for nonfunctional ones - has been the goal of researchers working in several muscular dystrophies, spinal muscular atrophy, Friedreich's ataxia, metabolic muscle diseases and myotubular myopathy.