National Institute of Neurological Disorders and Stroke (NINDS)

An informational video describes an ongoing National Institutes of Health study of natural history and biomarkers in spinal muscular atrophy

posted on February 13, 2013 - 9:41am
Update (April 2, 2014): As of March 31, 2014, the investigators were seeking four SMA-affected infants. Update (Jan. 9, 2014): As of Dec. 30, 2013, the investigators were seeking eight SMA-affected infants.

The SMA Project, a National Institutes of Health program supported by SMA patient advocacy groups, reports on its therapy development strategy in spinal muscular atrophy

posted on December 24, 2012 - 5:00am
A small-molecule drug candidate for spinal muscular atrophy (SMA) and an effective strategy for advancing therapy development are the primary outcomes being reported by the Spinal Muscular Atrophy (SMA) Project, a program established in 2003 by the National Institute of Neurological Disorders and Stroke (NINDS) to accelerate the development of therapeutic candidates for thi