An informational video describes an ongoing National Institutes of Health study of natural history and biomarkers in spinal muscular atrophy
posted on February 13, 2013 - 9:41am
Update (April 2, 2014): As of March 31, 2014, the investigators were seeking four SMA-affected infants.
Update (Jan. 9, 2014): As of Dec. 30, 2013, the investigators were seeking eight SMA-affected infants.
The SMA Project, a National Institutes of Health program supported by SMA patient advocacy groups, reports on its therapy development strategy in spinal muscular atrophy
posted on December 24, 2012 - 5:00am
A small-molecule drug candidate for spinal muscular atrophy (SMA) and an effective strategy for advancing therapy development are the primary outcomes being reported by the Spinal Muscular Atrophy (SMA) Project, a program established in 2003 by the National Institute of Neurological Disorders and Stroke (NINDS) to accelerate the development of therapeutic candidates for thi