Nan Sook Lee

Can toxic genes be blocked to treat disease?

posted on January 1, 2007 - 3:02pm
Since the 1990s, gene therapy - the insertion of functional genes to compensate for nonfunctional ones - has been the goal of researchers working in several muscular dystrophies, spinal muscular atrophy, Friedreich's ataxia, metabolic muscle diseases and myotubular myopathy.

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