MBNL1; muscleblind 1; CUG triplet repeat; Benjamin Miller; Charles Thornton

Freeing MBNL1 protein from RNA trap seen as step toward MMD1 treatment

posted on January 7, 2009 - 1:04pm
The identification of small molecules that can block the genetic defect that causes type 1 myotonic dystrophy (MMD1, or DM1) may be the first step toward developing a new drug treatment for the disease, say researchers at the University of Rochester (N.Y.) Medical Center (URMC). The abnormality that underlies MMD1 is a stretch of genetic material derived from DNA on chromosome 19 that contains...

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