Genethon

MDA partnered with a French muscle disease association to host a symposium on advancing gene therapy for neuromuscular diseases

posted on May 23, 2013 - 5:00am
Planning for the next generation of gene and stem cell therapies for muscular dystrophies — even as the first generation is still under development — was the theme of a joint symposium sponsored by MDA and the Association Française Contre les Myopathies (French Association Against Myopathies, or AFM) at the 16th annual meeting of the American Society of Gene & Cell Therapy (ASGCT).

Wake Forest researcher receives $369,365 for preclinical testing of gene transfer therapy for myotubular myopathy

posted on May 26, 2011 - 2:16pm
MDA’s translational research program has announced it is funding research into a potential treatment for the inherited muscle disorder X-linked myotubular myopathy (MTM). The grant of $369,365 grant to Wake Forest University professor Martin Childers will fund a three-year study of myotubularin gene transfer in mice and dogs that have an MTM-like disease.