gene therapy trial in LGMD

Five of six people with limb-girdle muscular dystrophy type 2D produced protein from the new genes

posted on October 29, 2010 - 2:25pm
Results from an MDA-supported, phase 1 study of gene therapy for the type 2D form of limb-girdle muscular dystrophy (LGMD2D) show sustained protein production from the transferred genes in two out of three trial participants six months after injection of the genes into a foot muscle. The new results follow an announcement last year showing protein production from transferred genes in the first...

New content is being added every day. Please check back again.