cell transplantation

posted on September 1, 2008 - 10:07am
Real progress is being made in supplying functional dystrophin genes to treat Duchenne muscular dystrophy (DMD), a disease in which mutated dystrophin genes keep this critical protein from being produced in muscle fibers.
posted on September 1, 2006 - 10:36am
QUEST Vol. 13, No. 5
Researchers, including MDA grantees, working on gene therapy for muscle and nerve diseases presented findings and exchanged ideas at the ninth annual meeting of the American Society of Gene Therapy, held in Baltimore in June. Improved cell therapy has promise, drawbacks