biostrophin

A report on drug development in neuromuscular diseases as of January 2009

posted on January 1, 2009 - 2:37pm
In the era of molecular biology, the drug development process has moved from a “let’s try it and see what happens” approach to a scientifically based process of discovery and application. For many of the diseases in MDA’s program, drug discovery begins with gene discovery — identifying a gene that, when flawed, causes a disease.
posted on May 1, 2007 - 8:47pm
QUEST Vol. 14, No. 3
Items in this article report on clinical trials in: Duchenne muscular dystrophy and Friedreich's ataxia.
posted on March 29, 2006 - 10:51am
The first U.S. human gene therapy trial directed at Duchenne muscular dystrophy (DMD) was launched yesterday at Columbus (Ohio) Children's Hospital, the Muscular Dystrophy Association (MDA), Children’s Hospital, and Asklepios Biopharmaceutical Inc. (AskBio) announced today.  Neurologist Jerry Mendell administered an injection of AskBio’s Biostrophin, which contains a functional gene for the...