acid maltase enzyme

Four children not making any acid maltase enzyme tolerated enzyme replacement therapy when also treated with immunosuppressants

posted on January 16, 2012 - 6:00am
Editor's note 2/2/12: This story was updated to reflect the award of a  new MDA grant to Eric Sjoberg at Amicus Therapeutics. Drugs that suppress the immune system can successfully prevent or reverse rejection of enzyme replacement therapy in Pompe disease (acid maltase deficiency), a new study has shown.
posted on July 1, 2008 - 1:37pm
QUEST Vol. 15, No. 4
This article includes items on: Duchenne muscular dystrophy, myotubular myopathy, acid maltase deficiency, spinal muscular atrophy, genetic information, limb-girdle muscular dystrophy, congenital muscular dystrophy, translational research