AAV8 vectors

Researchers funded in part by MDA found that a single blood-vessel injection of myotubularin genes markedly improved muscle abnormalities and survival in mice and dogs

posted on January 22, 2014 - 12:03pm
Update (Feb. 3, 2014): The video from the University of Washington has been edited, and the link has been updated to reflect this. Update (Jan. 27, 2014): MDA also supported Alan Beggs at Harvard University on this study. We regret not including this information intially.

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