48 week results

Trial results for the Duchenne MD drug eteplirsen show real improvements in dystrophin production and walking ability

posted on October 3, 2012 - 5:53pm
Update (Aug. 8, 2013): This story has been updated to reflect the Aug. 1, 2013, publication of these results in Annals of Neurology.

A trial of the exon-skipping drug eteplirsen resulted in an increase in both dystrophin production and walking ability in boys with Duchenne MD

posted on October 3, 2012 - 5:45am
Update (Aug. 8, 2013): This story has been updated to reflect the Aug. 1, 2013, publication of these trial results in Annals of Neurology.