IDMC-8, held Nov. 30-Dec. 3, 2011, explored disease mechanisms, clinical aspects and ideas for future therapies in myotonic muscular dystrophy
posted on December 8, 2011 - 3:05pm
The 8th International Myotonic Dystrophy Consortium Meeting (IDMC-8), was an exciting mix of the latest scientific developments and clinical research in types 1 and 2 myotonic dystrophy (MMD1 and MMD1, also known as DM1 and DM2).
A new, NIH-supported translational research center will focus on exon skipping as a treatment for MD
posted on October 19, 2011 - 5:00am
A Center for Research Translation of Systemic Exon Skipping in Muscular Dystrophy has been established by the National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS), part of the U.S. National Institutes of Health.
The search for therapies and cures must be accompanied by the cultivation of the best and brightest researchers
posted on October 1, 2011 - 3:33pm
All MDA grants have the same basic goal: moving promising treatments through the “drug development pipeline,” from early discoveries in the lab, to clinical trials, to actual therapies that can be prescribed in the clinic.
But some MDA grants are designed to accomplish this goal not only by funding research but by encouraging the “best and the brightest” young scientists to become future...
posted on July 1, 2011 - 1:01pm
New CMS-causing genetic mutations indentified
Scientists supported in part by MDA have identified mutations in the gene for the plectin protein as a rare cause of a congenital myasthenic syndrome (CMS).
An MDA-sponsored meeting explored progress in five key therapeutic strategies under development for neuromuscular diseases
posted on March 18, 2011 - 3:30pm
Moving therapeutic strategies from the laboratory to clinical trials and ultimately to the market as treatments was the theme of the MDA National Scientific Conference held March 13-16, 2011, in Las Vegas.
Some 300 people attended the conference, the first in a planned series of such MDA-sponsored meetings that will emphasize new research and current medical care. The majority of presenters and...
University of Illinois-Chicago scientist receives $530,480 to test immune-system modulator for myasthenia gravis
posted on March 14, 2011 - 3:51pm
MDA’s translational research program has announced it is funding research into a potential treatment for the autoimmune disorder myasthenia gravis (MG).
The grant of $530,480 to University of Illinois-Chicago professor Matthew Meriggioli will fund a three-year study of an immune-system modulator called GM-CSF. The compound will be tested in a mouse model of MG and in a small group of human...
MDA has awarded 44 new grants aimed at uncovering the underlying molecular causes of, and developing therapies for, many of the diseases in its program
posted on February 4, 2011 - 1:22pm
The Muscular Dystrophy Association has awarded 44 grants totaling $13.5 million to support research efforts aimed at advancing understanding of disease processes and uncovering new strategies for treatments and cures of muscular dystrophy and the more than 40 other diseases in the Association’s program.
The new grants were reviewed by MDA’s Scientific and Medical Advisory Committees, and approved...